
Search Clinical Trials
The U.S. National Library of Medicine provides a database of clinical trials worldwide. Use the fields below to search the database. Expand your results and select terms or phrases and right-click to search using Google, MalaCards, MedlinePlus, PubMed, or Wikipedia.
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Clinical Trials Search Results
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Count: 14
Selected: 0
NCT ID | Title | ||
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NCT04283227 | OTL-200 in Patients With Late Juvenile Metachromatic Leukodystrophy (MLD) | ||
NCT01560182 | Gene Therapy for Metachromatic Leukodystrophy (MLD) | ||
NCT05687474 | Baby Detect : Genomic Newborn Screening | ||
NCT05354219 | Validation and Reliability of Iris Cameras in Mucopolysaccharidoses | ||
NCT03047369 | The Myelin Disorders Biorepository Project | ||
NCT05368038 | ScreenPlus: A Comprehensive, Flexible, Multi-disorder Newborn Screening Program | ||
NCT03765632 | Efficacy and Safety of the Cryopreserved Formulation of OTL-101 in Subjects With ADA-SCID | ||
NCT06149403 | A Study to Investigate the Efficacy and Safety of OTL-203 in Subjects with MPS-IH Compared with Standard of Care with Allogeneic HSCT | ||
NCT01380990 | Lentiviral (LV) Gene Therapy for Adenosine Deaminase (ADA) Deficiency | ||
NCT02999984 | Efficacy and Safety of the Cryopreserved Formulation of OTL-101 in Subjects With ADA-SCID | ||
NCT04201405 | Gene Therapy With Modified Autologous Hematopoietic Stem Cells for Patients With Mucopolysaccharidosis Type IIIA | ||
NCT01852071 | Autologous CD34+ Hematopoietic Stem Cells Transduced ex Vivo With Elongation Factor 1 Alpha Shortened (EFS) Lentiviral Vector Encoding for the Human ADA Gene | ||
NCT02453477 | Gene Therapy for Transfusion Dependent Beta-thalassemia | ||
NCT03392987 | A Safety and Efficacy Study of Cryopreserved OTL-200 for Treatment of Metachromatic Leukodystrophy (MLD) |