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The U.S. National Library of Medicine provides a database of clinical trials worldwide. Use the fields below to search the database. Expand your results and select terms or phrases and right-click to search using Google, MalaCards, MedlinePlus, PubMed, or Wikipedia.
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Clinical Trials Search Results
Search History:
Count: 16
Selected: 0
NCT ID | Title | ||
---|---|---|---|
NCT04105166 | Gene Therapy for Pyruvate Kinase Deficiency (PKD) | ||
NCT03766386 | The Natural History of Danon Disease | ||
NCT03812263 | A Clinical Trial to Evaluate the Safety and Efficacy of RP-L201 in Subjects With Leukocyte Adhesion Deficiency-I | ||
NCT04248439 | Gene Therapy for Fanconi Anemia, Complementation Group A | ||
NCT06092034 | A Gene Therapy Study of RP-A501 in Male Patients With Danon Disease | ||
NCT05885412 | A Phase 1, Dose Escalation Trial of RP-A601 in Subjects With PKP2 Variant-Mediated Arrhythmogenic Cardiomyopathy (PKP2-ACM) | ||
NCT05548855 | Natural History of Danon Disease | ||
NCT03814408 | A Clinical Trial to Evaluate the Safety of RP-L102 in Pediatric Subjects With Fanconi Anemia Subtype A | ||
NCT06282432 | Long-Term Follow-Up (LTFU) for Gene Therapy of Leukocyte Adhesion Deficiency-I (LAD-I) | ||
NCT03882437 | Gene Therapy for Male Patients With Danon Disease (DD) Using RP-A501; AAV9.LAMP2B | ||
NCT04525352 | A Trial to Evaluate Safety and Efficacy of RP-L401-0120 in Subjects With Infantile Malignant Osteopetrosis | ||
NCT06214507 | Danon Disease Natural History Study | ||
NCT04069533 | Lentiviral-mediated Gene Therapy for Pediatric Patients With Fanconi Anemia Subtype A | ||
NCT06422351 | Clinical Trial to Evaluate the Efficacy of Gene Therapy for Pyruvate Kinase Deficiency | ||
NCT04437771 | Long-Term Follow-up of Subjects With Fanconi Anaemia Subtype A Treated With ex Vivo Gene Therapy | ||
NCT03825783 | A Gene Therapy Trial to Evaluate the Safety and Efficacy of RP-L201 in Subjects With Leukocyte Adhesion Deficiency-I |