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The U.S. National Library of Medicine provides a database of clinical trials worldwide. Use the fields below to search the database. Expand your results and select terms or phrases and right-click to search using Google, MalaCards, MedlinePlus, PubMed, or Wikipedia.

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Clinical Trials Search Results

Query: "TILT[LastUpdatePostDate]SEARCH[Study]AREA[SponsorSearch]Spark Therapeutics"
Count: 14
Selected: 0
NCT IDTitle
NCT02341807Safety and Dose Escalation Study of AAV2-hCHM in Subjects With CHM (Choroideremia) Gene Mutations
NCT04093349A Gene Transfer Study for Late-Onset Pompe Disease (RESOLUTE)
NCT03893240Neutralizing Antibody Seroprevalence Study With a Retrospective Component in Participants With Late-Onset Pompe Disease
NCT03597399A Patient Registry Study for Patients Treated With Voretigene Neparvovec in US
NCT03003533A Gene Transfer Study for Hemophilia A
NCT01208389Phase 1 Follow-on Study of AAV2-hRPE65v2 Vector in Subjects With Leber Congenital Amaurosis (LCA) 2
NCT03432520Long-Term Safety and Efficacy of SPK-8011 in Males With Hemophilia A
NCT03734588Dose-finding Study of SPK-8016 Gene Therapy in Patients With Hemophilia A to Support Evaluation in Individuals With FVIII Inhibitors
NCT03602820Long-term Follow-up Study in Subjects Who Received Voretigene Neparvovec-rzyl (AAV2-hRPE65v2)
NCT03876301Lead-in Study to Collect Prospective Efficacy and Safety Data of Current FVIII Prophylaxis Replacement Therapy in Adult Hemophilia A Participants
NCT00516477Safety Study in Subjects With Leber Congenital Amaurosis
NCT00999609Safety and Efficacy Study in Subjects With Leber Congenital Amaurosis
NCT00515710LTFU for Gene Transfer Subjects With Hemophilia B
NCT01620801Hemophilia B Gene Therapy With AAV8 Vector