
Search Clinical Trials
The U.S. National Library of Medicine provides a database of clinical trials worldwide. Use the fields below to search the database. Expand your results and select terms or phrases and right-click to search using Google, MalaCards, MedlinePlus, PubMed, or Wikipedia.
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Clinical Trials Search Results
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Count: 16
Selected: 0
NCT ID | Title | ||
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NCT03602820 | Long-term Follow-up Study in Subjects Who Received Voretigene Neparvovec-rzyl (AAV2-hRPE65v2) | ||
NCT03432520 | Long-Term Safety and Efficacy of Spark-Sponsored Gene Therapies in Males With Hemophilia A | ||
NCT01620801 | Hemophilia B Gene Therapy With AAV8 Vector | ||
NCT03876301 | Lead-in Study to Collect Prospective Efficacy and Safety Data of Current FVIII Prophylaxis Replacement Therapy in Adult Hemophilia A Participants | ||
NCT01208389 | Phase 1 Follow-on Study of AAV2-hRPE65v2 Vector in Subjects With Leber Congenital Amaurosis (LCA) 2 | ||
NCT03893240 | Neutralizing Antibody Seroprevalence Study With a Retrospective Component in Participants With Late-Onset Pompe Disease | ||
NCT06297486 | Study of a Gene Therapy Treatment for Hemophilia A | ||
NCT06826612 | A Randomized Study of SPK-10001 Gene Therapy in Participants With Huntington's Disease | ||
NCT00515710 | LTFU for Gene Transfer Subjects With Hemophilia B | ||
NCT03597399 | A Patient Registry Study for Patients Treated With Voretigene Neparvovec in US | ||
NCT04093349 | A Gene Transfer Study for Late-Onset Pompe Disease (RESOLUTE) | ||
NCT00999609 | Safety and Efficacy Study in Subjects With Leber Congenital Amaurosis | ||
NCT02341807 | Safety and Dose-escalation Study of AAV2-hCHM in Participants With CHM (Choroideremia) Gene Mutations | ||
NCT03734588 | Dose-finding Study of SPK-8016 Gene Therapy in Patients With Hemophilia A to Support Evaluation in Individuals With FVIII Inhibitors | ||
NCT00516477 | Safety Study in Subjects With Leber Congenital Amaurosis | ||
NCT03003533 | A Gene Transfer Study for Hemophilia A |